1st Faculty of Medicine Charles University 1st Faculty of Medicine Charles University ADENYLOSUCCINATE LYASE DEFICIENCY
zikanova 17.09.2026

ADSL deficiency

 Adenylosuccinate lyase (ADSL) deficiency is a rare inherited disorder of de novo purine synthesis with predominantly neurological manifestations.

This section provides information about ADSL deficiency for patients, families, clinicians and researchers, together with our databases of published patients and reported ADSL variants. 

Patients & families

Information about ADSL deficiency, diagnosis, treatment and current research written for patients and families.

Patients & families →

Professionals

Clinical, biochemical and molecular information on ADSL deficiency for clinicians, diagnostic laboratories and researchers.

Professional overview →

Patient database

A curated overview of published patients with ADSL deficiency, including available clinical, biochemical and genetic information.

Open patient database →

Variant database

An overview of reported disease-associated variants in the ADSL gene.

Open variant database →

number of views: 25 author: zikanova, last modification: zikanova, 17.09.2026